Saturday, May 11 2024
11:00 AM – 11:15 AM ET - Room 307-308
397: Correction of Myotonia and Reduction of Toxic DMPK Foci After Treatment of the HSALR Mouse Model of Myotonic Dystrophy Type 1 Using an Adeno-Associated Virus Delivering U7snRNA Interfering with CTG Repeat Expansion
Nicolas Wein - PhD
Abigail Wexner Research Institute at Nationwide Children's Hospital