Session Details

Speakers, titles, times, and locations of ASGCT presentations

Detailed Program

Delivery & Development of Precision Genome Editing Technologies

In this workshop, we will focus on the intersection between the engineering, delivery, and in vivo application of genome editing tools. We will discuss how novel delivery research drives innovation and need for new genome editing strategies, and vice versa. Attendees of this workshop can hope to learn about the most recent applications of a variety of genome editors across a broad range of target cell and organ systems.

Session Details



In vivo gene editing in porcine models of heart disease, also in comparison to “classic” AAV gene therapy

Leveraging on the LNP/mRNA technology for ex-vivo gene editing

Next generation epigenetic editing

In vivo gene editing with virus-like particles

LNP development and screening

Development and delivery of prime editors

In vivo AAV delivery for genome editing

Fanzor is a eukaryotic programmable RNA-guided endonuclease

Programmable multi-kilobase RNA editing using CRISPR-mediated trans-splicing

Computational design of sequence-specific DNA-binding proteins

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