Agenda Details

Learn more about sessions and presentations at the 26th Annual Meeting

Detailed Program

Advancing Novel Delivery Tools and Treatments for Neurodegenerative Disorders

There is an urgent need to investigate therapeutic strategies and novel treatments for genetic or acquired neurodegenerative disorders. To this end, important issues related to the effective delivery and biodistribution of the therapeutic product/s in target tissues, the durability of the beneficial effects as well as the potential toxicity of the procedure and/or products have to be carefully evaluated.

Session Details


Angela Gritti, PhD. San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Italy


Fredric Manfredsson. Barrow Neurological Institute, AZ


Megan S. Keiser, PhD. Children's Hospital of Philadelphia, Philadelphia, PA

Discovery and Characterization of Novel Cross-Species BBB-Penetrant Capsids

Brett Hoffman, PhD. Voyager Therapeutics, Cambridge, MA

Exosomes for delivery to the CNS

Dhanu Gupta. University of Oxford, Oxford, United Kingdom

A Novel Delivery Approach to Support Development of Genetic Medicines for Human Inner Ear Conditions

Michelle D. Valero, PhD. Akouos, a wholly owned subsidiary of Eli Lilly, MA

Pushing the Envelope: Will Novel Gene Knockdown Strategies Get us to a Cure for Motor Neuron Disease?

Defne Amado, MD, PHD. University of Pennsylvania, PA

This site uses cookies to offer you a better user experience and to analyze site traffic. By continuing to use this website, you accept our use of cookies.