Session Details

Speakers, titles, times, and locations of ASGCT presentations

Detailed Program

Gene Editing Technologies (Organized by the Education Committee)

The CRISPR field has evolved to safer systems with lower off-target effects, and human trials are showing efficacy in vivo. An update of current base-editing methods and specific in vivo approaches to treat genetic diseases will be covered.

Learning Objectives: (3-4 preferred)

  • Basics of gene editing
  • Mechanisms of different CRISPR/Cas systems
  • Basis for disease treatment using CRISPR (CF and Transthyretin Amyloidosis)

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