Session Details

Session Details

01:30 PM - 03:15 PM - Ballroom 1

David Segal - PhD - UC Davis Genome Center

Co-Chair

01:30 PM - 03:15 PM - Ballroom 1

Samuele Ferrari - PhD - SR-TIGET

Co-Chair

01:30 PM - 01:45 PM - Ballroom 1

Michelle LeBlanc - PhD - SalioGen Therapeutics

11: Efficacy and Integration of a Non-Viral ABCA4 Transposon in Treating Stargardt Disease: Evidence from Mice and Primate Studies

01:45 PM - 02:00 PM - Ballroom 1

Kartika Venugopal - Tessera Therapeutics

12: RNA-Based Gene Writer and Lipid Nanoparticle (LNP) Delivery Enables Generation of Functional Chimeric Antigen Receptor (CAR) T Cells with In Vitro and In Vivo Anti-Tumor Activity and T Cell-Specific Genome Engineering In Vivo

02:00 PM - 02:15 PM - Ballroom 1

Peter Cameron - Profluent Bio

13: Language Models Generate Novel Genome Editors from Scratch

02:15 PM - 02:30 PM - Ballroom 1

Inna Shcherbakova - ReNAgade Therapeutics

14: Retron Mediated Exon-Sized Genome Insertion Using an All- RNA System

02:30 PM - 02:45 PM - Ballroom 1

Lucas Harrington - Mammoth Biosciences

15: Reduction in Triglycerides through a Novel Ultracompact CRISPR System: Efficacy in Mouse Models and NHP Studies

02:45 PM - 03:00 PM - Ballroom 1

Claudia Huichalaf - PhD - Alexion AstraZeneca Rare Disease

16: Selective Repression of C9ORF72 Repeat Expansion-Containing Sense and Antisense Transcripts in an ALS Mouse Model

03:00 PM - 03:15 PM - Ballroom 1

Di Yin - PhD - Stanford University

17: Systematic Discovery, In Vivo Delivery, and DNA Repair Mechanism of Single-Strand Annealing Protein for Precision Integration of Large DNA Sequences