Agenda Details | ASGCT Annual Meeting

Detailed Program

Wednesday, May 17 2023
08:00 AM – 09:45 AM PT

Gene Editing Technologies

This session will cover an overview of CRISPR/Cas9 technologies and safety issues, how to select guide RNAs, as well as provide advances in the treatment of human diseases.Learning Objectives for this session:Understand the principles of CRISPR/Cas9 genome editing and its safety considerations.Understand the principles of Prime editing and its clinical applications in neurodegenerative diseases.

Session Details

08:00 AM – 09:45 AM - Petree Hall D

Co-Chair

Kimberly Nye. TESS Research Foundation, Menlo Park, CA

08:00 AM – 09:45 AM - Petree Hall D

Co-Chair

Renata Stripecke, PhD. University of Cologne, Germany

08:01 AM – 08:30 AM - Petree Hall D

CRISPR off-target activity and mitigation strategies

Kyle Cromer, PhD. UCSF, CA

08:30 AM – 09:00 AM - Petree Hall D

Prime editing corrections of point mutations responsible for Duchenne Muscular Dystrophy, Central Core Disease, Ataxia-8 and malignant hyperthermia

Jacques P. Tremblay, PhD. Laval University, Québec, QC, Canada

09:00 AM – 09:30 AM - Petree Hall D

CRISPR-derived Genome Editing Therapies: Progress from Bench to Bedside

Zoya Gluzman-Poltorak, PhD, MBA. SonoThera, San Francisco, CA