Tuesday, May 7

8 a.m. - 12 p.m.

Workshops

Why do Rare Disease Clinical Trials Often Miss the Mark? Best Practices and Approaches to Optimize Design of Rare Disease Clinical Trials

Revolutionizing Care: Gene Therapy Unveiled for Clinicians

1:30 p.m. - 3:15 p.m.

Oral Abstract Session

Lysosomal Storage Diseases

Wednesday, May 8

8 a.m. - 9:45 a.m.

Oral Abstract Session

Clinical Trials Spotlight

Education Session

Clinical Translation of Gene and Cell Therapies

Scientific Symposium

From the Clinic Back to the Bench: Solving Old Problems with New Technologies

1:30 p.m. - 3:15 p.m.

Scientific Symposium

Bespoke Gene Therapy Consortium

3:45 p.m. - 5:30 p.m.

Scientific Symposium

Bespoke Gene Therapy Consortium

Oral Abstract Session

Strategies and Technologies for Advanced CMC

Thursday, May 9

8 a.m. - 9:45 a.m.

Scientific Symposium

Lessons Learned from Clinical Efficacy and Safety of Gene and Cell Therapies

1:30 p.m. - 3:15 p.m.

Oral Abstract Session

In-Vivo Gene Therapy Clinical Trials

3:45 p.m. - 5:30 p.m.

Education Session

Education and Regulations in Gene and Cell Therapy

Friday, May 10

8 a.m. - 9:45 a.m.

Scientific Symposia

Therapeutic Vaccines for Persistent Viral Infections and Cancer

Collaboration Models for Global Gene Therapy

1:30 p.m. - 3:15 p.m.

Oral Abstract Session

Cell Therapy and Cell-Based Gene Therapy Trials

3:45 p.m. - 5:30 p.m.

Oral Abstract Session

AAV Vectors - Product Development, Manufacturing, and Approval Considerations Session 4

Saturday, May 11

8 a.m. - 9:45 a.m.

Scientific Symposium

Pressing Clinical Challenges in Gene Therapy

10:15 a.m. - 12 p.m.

Oral Abstract Sessions

Vector Product Engineering, Development, and Manufacturing (excluding AAV)

Molecular and Cellular Methods and Technologies