A Focus on Gene and Cell Therapy for Clinicians
All times below listed in ET
Planned by the Clinician Education Working Group. Held in collaboration with the National Organization for Rare Disorders (NORD).
Register for A Focus on Gene and Cell Therapy for Clinicians
8:00 – 8:20 a.m.
A Focus on Gene and Cell Therapy for Clinicians - Introduction: What Therapies Are Available Today?
Terence R. Flotte, MD, UMass Chan Medical School
8:20 – 8:45 a.m.
Types of Therapies – Lentiviral/In-vivo HSC
Matthew Porteus, MD, PhD, Stanford University
8:45 – 9:10 a.m.
Types of Therapies – AAV
Jerry R. Mendell, MD, PhD, The Research Institute at Nationwide Children's Hospital
9:10 – 9:35 a.m.
Types of Therapies – CAR-T Therapies
David L. Porter, MD, Hospital of the University of Pennsylvania
9:35 – 10:00 a.m.
Clinical Trials and My Role - How Do I Find a Clinical Trial?
Florian Eichler, MD, Massachusetts General Hospital
10:00 – 10:25 a.m.
Clinical Trials and the Role of FDA - Identifying Definitive Clinical Outcomes
Peter Marks, FDA
10:25 – 11:05 a.m.
Running a Clinical Trial
Kathryn Wagner, MD, PhD
11:05 – 11:30 a.m.
Ethics of Recommending a Clinical Trial
Alison Bateman-House, PhD, MPH
11:30 – 11:55 a.m.
Hospital Pharmacy Role in Managing Insurance Issues
Michael Storey, PharmD, Nationwide Children’s Hospital