Agenda Details

Learn more about sessions and presentations at the 25th Annual Meeting

Detailed Program

Gene Therapy Beyond Cancer (Organized by the Education Committee)

The morbidity and mortality of refractory cancers have allowed expedited clinical translation of many gene and cell therapy approaches. The success of the chimeric antigen receptor T (CAR-T) cell technology has inspired a new generation of researchers and intensified efforts and resources focused on gene and cell therapeutic approaches. Many rare inherited diseases represent the next frontier for such approaches, with many diseases currently lacking therapeutic options. On targeting such diseases, however, new challenges are presented, from obscure pathophysiologic pathways to complex delivery systems. These investigations will not only lead to promising therapies for orphan diseases, but also further develop research models and technologies for gene and cell therapy approaches.

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