Agenda Details

Learn more about sessions and presentations at the 25th Annual Meeting

Detailed Program

Finding a “Cure”: The Promise and Perils of Gene Therapy, In Utero and Beyond (Organized by the Gene and Cell Therapy of Genetic and Metabolic Diseases Committee)

This session will review selective milestones in the early treatment of genetic and metabolic disorders as well as overview the landscape of newborn screening from the public health and care perspectives. The rationale is to update the community on developments in the space of early in life gene therapy studies spanning the translational spectrum needed to fully explore the benefits and risk of early treatment for genetic disorders.

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