Immerse yourself in CGT policy discussions at the Policy Summit, Sept. 18-19!
Learn more about sessions and presentations at the 26th Annual Meeting
Saturday, May 20 2023 10:15 AM – 12:00 PM PT
Transfer RNAs (tRNA) play a critical role in decoding mRNAs into proteins. These small ~76-90 nt RNA molecules function as cellular couriers and bring a specific amino acid to the ribosome complex that corresponds to the intended mRNA codon. A growing body of evidence implicates that engineered tRNAs can be used as therapeutic molecules to suppress premature stop codons and insert functional amino acids. In addition, emerging data suggest a pathobiological role of fragmented tRNAs in human diseases. This session will cover a range of topics from genetics of tRNAs to their pathophysiology and therapeutic use.
10:15 AM – 12:00 PM - Room 515 AB
Mark A.. Kay, MD, PhD. Stanford University School of Medicine, Stanford, CA
Paloma H.. Giangrande, PhD. Wave Life Sciences, Cambridge, MA
Shen Shen, PhD. Vertex Pharmaceuticals, Boston, MA
Janaiah Kota. Ultragenyx, IN
10:16 AM – 10:40 AM - Room 515 AB
Todd M. Lowe, PhD. University of California Santa Cruz, CA
10:40 AM – 11:05 AM - Room 515 AB
Saumya Das, MD, PhD. Massachusetts General Hospital, Boston, MA
11:05 AM – 11:30 AM - Room 515 AB
Theonie Anastassiadis. Alltrna, MA, Flagship Pioneering, MA
11:30 AM – 11:55 AM - Room 515 AB
Christopher Ahern, PhD. University of Iowa, IA
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